Nicola Brunetti-Pierri of the Telethon Institute of Genetics and Medicine joins the podcast to discuss his recent review looking at the various gene therapy approaches in the mucopolysaccharidoses along with their strengths and limitations.
Gene therapies for mucopolysaccharidoses
Alessandro Rossi and Nicola Brunetti-Pierri
https://doi.org/10.1002/jimd.12626
